RIVUNATPAGENE MIZIPARVOVEC
UNII 24Q8LJQ6Y2

Substance Identification & Data

This profile provides standardized clinical and technical data for Rivunatpagene Miziparvovec, uniquely identified by the FDA Unique Ingredient Identifier (UNII) 24Q8LJQ6Y2.

Technical mappings include the Chemical Abstracts Service (CAS) Registry Number 2646715-00-4 and the RxNorm Concept ID (RxCUI) N/A. Explore the sections below for detailed nomenclature and a complete directory of NDC-listed products containing this ingredient.

FDA UNII Code
24Q8LJQ6Y2
CAS Registry Number
2646715-00-4
RxNorm Concept ID
N/A

Detailed Substance Profile

Preferred Name
RIVUNATPAGENE MIZIPARVOVEC
Official standardized name for this substance within the FDA UNII nomenclature system.
NCI Thesaurus
National Cancer Institute reference terminology for clinical and research data.
INN ID
12388
Sequential identifier assigned via the WHO International Nonproprietary Name program.
USAN ID
MN-21
Identifier assigned by the United States Adopted Names Council.
Substance Type
structurallyDiverse
ISO 11238 classification category (e.g., Chemical, Polymer, Protein).

Synonyms and Nomenclature

This section provides a complete list of nomenclature and identifier mappings for Rivunatpagene Miziparvovec. Identifiers are organized into official regulatory terms, commercial trade names, and technical systematic synonyms used to ensure accurate identification across clinical pharmaceutical databases, regulatory filings, and electronic health records.

FDA Official Name

RIVUNATPAGENE MIZIPARVOVEC

Common Names & Synonyms

DNA (RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRUS SEROTYPE 9 VECTOR UX701 MURINE TRANSTHYRETIN ENHANCER PLUS HUMAN TRANSTHYRETIN PROMOTER PLUS SIMIAN VIRUS 40 INTRON PLUS HUMAN ADENOSINE TRIPHOSPHATASE COPPER-TRANSPORTING .BETA. METAL-BINDING DOMAIN 4/5/6 TRANSGENE ATP7B-MBD456 PLUS SIMIAN VIRUS 40 POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS PLUS ADENO-ASSOCIATED VIRUS 2 REP REGION PLUS ADENO-ASSOCIATED VIRUS 9 CAP REGION-SPECIFYING)
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING ATPASE COPPER-TRANSPORTING BETA GENE (ATP7B, COPPER TRANSPORTING ATPASE 2), MODIFIED TO ENCODE THE LAST THREE OF THE SIX METAL-BINDING DOMAINS (ATP7B-MBD456), UNDER CONTROL OF A MURINE TRANSTHYRETIN ENHANCER/HUMAN TRANSTHYRETIN PROMOTER, WITH A SIMIAN VIRUS 40 (SV40) INTRON, TERMINATED WITH AN SV40 POLYADENYLATION SIGNAL, AND FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS)
RIVUNATPAGENE MIZIPARVOVEC [INN]
RIVUNATPAGENE MIZIPARVOVEC [USAN]
UX-701

Technical Codes

UX701