SESICLENEGENE COSAPARVOVEC
UNII 53A6SJF4WE

Substance Identification & Data

This profile provides standardized clinical and technical data for Sesiclenegene Cosaparvovec, uniquely identified by the FDA Unique Ingredient Identifier (UNII) 53A6SJF4WE.

Technical mappings include the Chemical Abstracts Service (CAS) Registry Number 2379806-98-9 and the RxNorm Concept ID (RxCUI) N/A. Explore the sections below for detailed nomenclature and a complete directory of NDC-listed products containing this ingredient.

FDA UNII Code

53A6SJF4WE

CAS Registry Number

2379806-98-9

RxNorm Concept ID

N/A

Detailed Substance Profile

Preferred Name

SESICLENEGENE COSAPARVOVEC

Official standardized name for this substance within the FDA UNII nomenclature system.

NCI Thesaurus

C179119

National Cancer Institute reference terminology for clinical and research data.

INN ID

11600

Sequential identifier assigned via the WHO International Nonproprietary Name program.

Substance Type

structurallyDiverse

ISO 11238 classification category (e.g., Chemical, Polymer, Protein).

Synonyms and Nomenclature

This section provides a complete list of nomenclature and identifier mappings for Sesiclenegene Cosaparvovec. Identifiers are organized into official regulatory terms, commercial trade names, and technical systematic synonyms used to ensure accurate identification across clinical pharmaceutical databases, regulatory filings, and electronic health records.

FDA Official Name

SESICLENEGENE COSAPARVOVEC

Common Names & Synonyms

A NON-REPLICATING SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS (SCAAV) VECTOR ENCODING HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN 6. A RECOMBINANT NON-REPLICATING SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS SEROTYPE 9 (SCAAV9) VECTOR, ENCODING HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN 6 (CLN6), UNDER THE CONTROL OF A HYBRID CMV ENHANCER/CHICKEN-BETA-ACTIN PROMOTER AND A BOVINE GROWTH HORMONE (BGH) POLYA SEQUENCE, WITH AN SV40 INTRON 5' TO THE TRANSGENE, AND FLANKED BY AAV2 INVERTED TERMINAL REPEATS (ITRS). THE VECTOR GENOME IS A HEAD-TO-HEAD, SELF-COMPLEMENTARY DIMER, WITH THE VECTOR GENOME CASSETTE LOCATED 5' OF THE MUTATED INTERNAL INVERTED TERMINAL REPEAT (.DELTA.-ITR) IN A REVERSE COMPLEMENTARY ORIENTATION AND 3' OF THE .DELTA.-ITR IN A FORWARD ORIENTATION.

DNA (SELF-COMPLEMENTARY ADENO-ASSOCIATED VIRUS 9 VECTOR AT-GTX-501 HUMAN CYTOMEGALOVIRUS ENHANCER PLUS CHICKEN .BETA.-ACTIN HYBRID PROMOTER PLUS HUMAN CEROID-LIPOFUSCINOSIS NEURONAL PROTEIN CLN6-SPECIFYING)

SESICLENEGENE COSAPARVOVEC [INN]

Technical Codes

AT-GTX-501

External Clinical & Regulatory Resources

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