NIMATPAGENE PARIPARVOVEC
UNII C4J4L5V7XS

Substance Identification & Data

This profile provides standardized clinical and technical data for Nimatpagene Pariparvovec, uniquely identified by the FDA Unique Ingredient Identifier (UNII) C4J4L5V7XS.

Technical mappings include the Chemical Abstracts Service (CAS) Registry Number 2773545-20-1 and the RxNorm Concept ID (RxCUI) N/A. Explore the sections below for detailed nomenclature and a complete directory of NDC-listed products containing this ingredient.

FDA UNII Code
C4J4L5V7XS
CAS Registry Number
2773545-20-1
RxNorm Concept ID
N/A

Detailed Substance Profile

Preferred Name
NIMATPAGENE PARIPARVOVEC
Official standardized name for this substance within the FDA UNII nomenclature system.
NCI Thesaurus
National Cancer Institute reference terminology for clinical and research data.
INN ID
12798
Sequential identifier assigned via the WHO International Nonproprietary Name program.
Substance Type
structurallyDiverse
ISO 11238 classification category (e.g., Chemical, Polymer, Protein).

Synonyms and Nomenclature

This section provides a complete list of nomenclature and identifier mappings for Nimatpagene Pariparvovec. Identifiers are organized into official regulatory terms, commercial trade names, and technical systematic synonyms used to ensure accurate identification across clinical pharmaceutical databases, regulatory filings, and electronic health records.

Common Names & Synonyms

CAPSOMERE, RECOMBINANT HUMAN ADENO-ASSOCIATED VIRUS AAV3B VIRAL CAPSID PROTEIN VP1-VP2-VP3 COMPLEX (1:2:7), HEXACONTAMER, COMPLEX WITH DNA (RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRUS SEROTYPE 3B VECTOR VTX-801 LIVER-SPECIFIC HUMAN .ALPHA.-1 ANTITRYPSIN PROMOTER PLUS HUMAN 57-486-COPPER TRANSPORTER ATP7B CODON-OPTIMIZED GENE PLUS RABBIT .BETA.-GLOBIN POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS) (1:1)
NIMATPAGENE PARIPARVOVEC
NIMATPAGENE PARIPARVOVEC [INN]
NIMATPAGENE PARIPARVOVEC [WHO-DD]
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 3B (RAAV3B) VECTOR, ENCODING A SHORTENED VERSION OF THE HUMAN COPPER-TRANSPORTING ATPASE 2 (ATP7B) (ALSO KNOWN AS ATPASE COPPER-TRANSPORTING BETA, WILSON DISEASE-ASSOCIATED PROTEIN) WHICH IS DEVOID OF THE FIRST FOUR OF THE SIX METAL BINDING SITES (MBS) (MINI-ATP7B), UNDER CONTROL OF A LIVER SPECIFIC HUMAN ALPHA-1 ANTITRYPSIN (AAT) PROMOTER AND A SYNTHETIC POLYADENYLATION SEQUENCE DERIVED FROM THE POLYADENYLATION SIGNAL OF THE RABBIT ?-GLOBIN GENE, AND FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS)

Technical Codes

VTX-801