ARVENACOGENE SANPARVOVEC
UNII KNP55LBJ2N

Substance Identification & Data

This profile provides standardized clinical and technical data for Arvenacogene Sanparvovec, uniquely identified by the FDA Unique Ingredient Identifier (UNII) KNP55LBJ2N.

Technical mappings include the Chemical Abstracts Service (CAS) Registry Number 2891724-48-2 and the RxNorm Concept ID (RxCUI) N/A. Explore the sections below for detailed nomenclature and a complete directory of NDC-listed products containing this ingredient.

FDA UNII Code
KNP55LBJ2N
CAS Registry Number
2891724-48-2
RxNorm Concept ID
N/A

Detailed Substance Profile

Preferred Name
ARVENACOGENE SANPARVOVEC
Official standardized name for this substance within the FDA UNII nomenclature system.
NCI Thesaurus
C211781
National Cancer Institute reference terminology for clinical and research data.
INN ID
13234
Sequential identifier assigned via the WHO International Nonproprietary Name program.
Substance Type
structurallyDiverse
ISO 11238 classification category (e.g., Chemical, Polymer, Protein).

Synonyms and Nomenclature

This section provides a complete list of nomenclature and identifier mappings for Arvenacogene Sanparvovec. Identifiers are organized into official regulatory terms, commercial trade names, and technical systematic synonyms used to ensure accurate identification across clinical pharmaceutical databases, regulatory filings, and electronic health records.

FDA Official Name

ARVENACOGENE SANPARVOVEC

Common Names & Synonyms

ARVENACOGENE SANPARVOVEC [INN]
CAPSOMERE, RECOMBINANT ADENO-ASSOCIATED VIRUS 5 VIRAL CAPSID PROTEIN VP1-VP2-VP3 COMPLEX (1:1:10), HEXACONTAMER, COMPLEX WITH DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS VECTOR PAAV-HFIXCO-V2 MUS MUSCULUS TRANSTYRETIN GENE PROMOTER PLUS HUMAN .BETA.-GLOBIN GENE INTRON FRAGMENT PLUS HUMAN PREPROBLOOD COAGULATION FACTOR IX (384-LEUCINE) CODON-OPTIMIZED GENE PLUS HUMAN SOMATOTROPIN GENE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS) (1:1)
RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 5 (AAV5) VECTOR ENCODING A CODON-OPTIMIZED GAIN OF FUNCTION VARIANT (PADUA VARIANT, R338L) OF HUMAN COAGULATION FACTOR IX (FIX), UNDER THE CONTROL OF A MURINE LIVER-SPECIFIC TRANSTHYRETIN (TTR) PROMOTER AND HUMAN GROWTH HORMONE POLYADENYLATION SIGNAL, FLANKED BY AAV2 INVERTED TERMINAL REPEATS. A HUMAN BETA-GLOBIN INTRON HAS BEEN INSERTED BETWEEN THE PROMOTER AND THE FIX CODING REGION. THE VIRUS VECTOR ALSO CONTAINS MUTATIONS IN THE VIRAL AAV5 CAPSID PROTEIN VP1 (S2A AND T711S)

External Clinical & Regulatory Resources

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