VERBRINACOGENE SETPARVOVEC
UNII KT8AC75KUX

Substance Identification & Data

This profile provides standardized clinical and technical data for Verbrinacogene Setparvovec, uniquely identified by the FDA Unique Ingredient Identifier (UNII) KT8AC75KUX.

Technical mappings include the Chemical Abstracts Service (CAS) Registry Number 2364604-87-3 and the RxNorm Concept ID (RxCUI) N/A. Explore the sections below for detailed nomenclature and a complete directory of NDC-listed products containing this ingredient.

FDA UNII Code

KT8AC75KUX

CAS Registry Number

2364604-87-3

RxNorm Concept ID

N/A

Detailed Substance Profile

Preferred Name

VERBRINACOGENE SETPARVOVEC

Official standardized name for this substance within the FDA UNII nomenclature system.

NCI Thesaurus

C175872

National Cancer Institute reference terminology for clinical and research data.

INN ID

11278

Sequential identifier assigned via the WHO International Nonproprietary Name program.

USAN ID

HI-191

Identifier assigned by the United States Adopted Names Council.

Substance Type

structurallyDiverse

ISO 11238 classification category (e.g., Chemical, Polymer, Protein).

Synonyms and Nomenclature

This section provides a complete list of nomenclature and identifier mappings for Verbrinacogene Setparvovec. Identifiers are organized into official regulatory terms, commercial trade names, and technical systematic synonyms used to ensure accurate identification across clinical pharmaceutical databases, regulatory filings, and electronic health records.

FDA Official Name

VERBRINACOGENE SETPARVOVEC

Common Names & Synonyms

A RECOMBINANT NON-REPLICATING ADENO-ASSOCIATED VIRUS OF A MODIFIED LIVER-TROPIC SEROTYPE (S3) (RAAV REP2-CAPS3) VECTOR, ENCODING A GAIN-OF-FUNCTION VARIANT (R338LPADUA) OF CODON-OPTIMISED HUMAN COAGULATION FACTOR IX (HFIX) UNDER THE CONTROL OF A LIVER-SPECIFIC PROMOTER (FRE1) COMPRISING A TRUNCATED VERSION OF THE HUMAN APOLIPOPROTEIN E LOCUS CONTROL REGION (I.E. ENHANCER) WITH A TRUNCATED VERSION OF THE HUMAN ALPHA-1-ANTITRYPSIN PROMOTE

DNA (RECOMBINANT ADENO-ASSOCIATED VIRUS AAVS3-FLT180A VECTOR HUMAN BLOOD-COAGULATION FACTOR IX PADUA-SPECIFYING)

VERBRINACOGENE SETPARVOVEC [INN]

VERBRINACOGENE SETPARVOVEC [USAN]