POZETALDOGENE ORMESPARVOVEC
UNII R5CJD8SH2N

Substance Identification & Data

This profile provides standardized clinical and technical data for Pozetaldogene Ormesparvovec, uniquely identified by the FDA Unique Ingredient Identifier (UNII) R5CJD8SH2N.

Technical mappings include the Chemical Abstracts Service (CAS) Registry Number 2764626-03-9 and the RxNorm Concept ID (RxCUI) N/A. Explore the sections below for detailed nomenclature and a complete directory of NDC-listed products containing this ingredient.

FDA UNII Code
R5CJD8SH2N
CAS Registry Number
2764626-03-9
RxNorm Concept ID
N/A

Detailed Substance Profile

Preferred Name
POZETALDOGENE ORMESPARVOVEC
Official standardized name for this substance within the FDA UNII nomenclature system.
NCI Thesaurus
C203115
National Cancer Institute reference terminology for clinical and research data.
INN ID
12672
Sequential identifier assigned via the WHO International Nonproprietary Name program.
USAN ID
MN-234
Identifier assigned by the United States Adopted Names Council.
Substance Type
structurallyDiverse
ISO 11238 classification category (e.g., Chemical, Polymer, Protein).

Synonyms and Nomenclature

This section provides a complete list of nomenclature and identifier mappings for Pozetaldogene Ormesparvovec. Identifiers are organized into official regulatory terms, commercial trade names, and technical systematic synonyms used to ensure accurate identification across clinical pharmaceutical databases, regulatory filings, and electronic health records.

FDA Official Name

POZETALDOGENE ORMESPARVOVEC

Common Names & Synonyms

DNA (RECOMBINANT REPLICATION-DEFECTIVE ADENO-ASSOCIATED VIRUS SEROTYPE 9 VECTOR SBT101 CYTOMEGALOVIRUS ENHANCER FUSION WITH CHICKEN .BETA.-ACTIN PROMOTER AND EXON 1PLUS CHIMERIC CHICKEN .BETA.-ACTIN AND RABBIT .BETA.-GLOBIN INTRON PLUS RABBIT .BETA.-GLOBIN EXON 3 PLUS 5'-UNTRANSLATED REGION PLUS HUMAN ATP-BINDING CASSETTE TRANSPORTER SUB-FAMILY D MEMBER 1 GENE ABCD1 PLUS 3'-UNTRANSLATED REGION PLUS SIMIAN VIRUS 40 POLYADENYLATION SIGNAL AND BOVINE GROWTH HORMONE POLYADENYLATION SIGNAL PLUS ADENO-ASSOCIATED VIRUS 2 INVERTED TERMINAL REPEAT FLANKS)
POZETALDOGENE ORMESPARVOVEC [INN]
POZETALDOGENE ORMESPARVOVEC [USAN]
RECOMBINANT, NON-REPLICATING ADENO-ASSOCIATED VIRUS SEROTYPE 9 (RAAV9) VECTOR ENCODING HUMAN ADENOSINE TRIPHOSPHATE (ATP)-BINDING CASSETTE SUB-FAMILY D MEMBER 1 (ABCD1, ALSO KNOWN AS ADRENOLEUKODYSTROPHY (ALD) PROTEIN) UNDER CONTROL OF A HUMAN CYTOMEGALOVIRUS (CMV) ENHANCER/CHICKEN .BETA.-ACTIN (CBA) PROMOTER PLUS A .BETA.-ACTIN EXON, A CHIMERIC CHICKEN .BETA.-ACTIN/RABBIT .BETA.-GLOBIN INTRON, AND A RABBIT .BETA.-GLOBIN EXON 3, TERMINATED WITH SIMIAN VIRUS 40 (SV40) AND BOVINE GROWTH HORMONE (BGH) POLYADENYLATION SIGNALS, AND FLANKED BY ADENO-ASSOCIATED VIRUS 2 (AAV2) INVERTED TERMINAL REPEATS (ITRS)

Technical Codes

SBT101
SBT-101

External Clinical & Regulatory Resources

CAS
Common Chemistry
NCATS
Inxight Drugs
NLM
DailyMed Products
NCATS
GSRS Full Record
NIH
NCI Thesaurus